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Architects: Small & Medium Size Business (SMBs), Product Development, De-Risking, Validation, Building Niche & Emerging Markets
Architects: Biotechnology_DNA, RNA, RNAi, siRNA & mRNA
ADARx Pharmaceuticals
Organization & Developments: ADARx Pharmaceuticals
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ADARx Pharmaceuticals
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2021: The company has nine programs in the works across genetic, cardiometabolic and central nervous system diseases. It is developing its first editing program for the treatment of alpha-1 antitrypsin deficiency, or AATD, a rare genetic disorder that can lead to lung and liver disease.
ADARx Pharmaceuticals is a genetic medicine company focusing on oligonucleotide therapeutics for inhibition, degradation and base editing of mRNA transcripts.
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Finance & Acquisition: ADARx Pharmaceuticals
Key People: ADARx Pharmaceuticals