DOPATREE
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DOPATREE
CONDITIONS / TYPES BY COMMON MEDICAL GROUPINGS
NEUROLOGY CONDITIONS-ALL (NEUROLOGICAL)
NEUROLOGY CONDITIONS / TYPES
MOVEMENT DISORDERS-ALL (MOTOR DISEASES, NEUROMUSCULAR, MUSCULAR, MUSCLE, MOTOR IMPAIRMENT)
MOVEMENT DISORDERS / LISTINGS
SPINAL MUSCULAR ATROPHY-ALL (SMA, RESPIRATORY DISTRESS, DIAPHRAGMATIC, DISTAL, RESPIRATORY FAILURE, WERDNIG-HOFFMAN DISEASE, DUBOWITZ DISEASE, KUGELBERG-WELANDER DISEASE, JUVENILE)
SPINAL MUSCULAR ATROPHY / PRODUCTS / APPROVED
SPINRAZA® (NUSINERSEN)
SPINRAZA / MARKET ACCESS
Parents
SPINRAZA® (NUSINERSEN)
Children
ICER. SPINAL MUSCULAR ATROPHY. AN ASSESSMENT OF ONASEMNOGENE ABEPARVOVEC AND NUSINERSEN FOR SPINAL MUCULAR ATROPHY (SMA). PUBLIC MEETING. MAR 2019.