DOPATREE
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DOPATREE
ORGANIZATIONS
GOVERNMENT ORGANIZATIONS-ALL (GOVT, GOV’T)
UNITED STATES GOVERNMENT ORGANIZATIONS / LISTINGS
US FOOD AND DRUG ADMINISTRATION (FDA)
DRUGS AND BIOLOGICS / RELATED / US
US FDA NEW MOLECULAR ENTITY APPROVALS (NME, NEW CHEMICAL ENTITIES, NBE, NEW BIOLOGICAL ENTITIES)
US FDA NEW MOLECULAR ENTITY APPROVALS / LISTINGS / 2017
DEFLAZACORT (EMFLAZA®)
DEFLAZACORT / MARKET ACCESS
Parents
DEFLAZACORT (EMFLAZA®)
Children
ICER. DUCHENNE MUSCULAR DYSTROPHY. AN ASSESSMENT OF DEFLAZACORT, ETEPLIRSEN, AND GOLODIRSEN FOR THE TREATMENT OF DUCHENNE MUSCULAR DYSTROPHY. PUBLIC MEETING. JUL 2019.