DOPATREE
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DOPATREE
CONDITIONS
CONDITIONS / TYPES BY COMMON MEDICAL GROUPINGS
RARE DISEASES-ALL (SYNDROMES, GENETIC CONDITIONS, ORPHAN DRUG DESIGNATIONS, INHERITED, SYNDROMES, MULTISYSTEM, INBORN ERRORS, CHROMOSOMAL, MULTIPLE DISORDERS, MULTI-SYSTEMS, ULTRA-RARE)
RARE DISEASES / TYPES
Parents
RARE DISEASES-ALL (SYNDROMES, GENETIC CONDITIONS, ORPHAN DRUG DESIGNATIONS, INHERITED, SYNDROMES, MULTISYSTEM, INBORN ERRORS, CHROMOSOMAL, MULTIPLE DISORDERS, MULTI-SYSTEMS, ULTRA-RARE)
Children
CHROMOSOMAL CONDITIONS-ALL (ANOMALY, ANOMALIES, ABERRATIONS, MUTATIONS, DEFECTS, CHROMOSOME, DISORDERS)
INBORN ERRORS OF METABOLISM-ALL (IEM)
LEUKODYSTROPHY CONDITIONS-ALL (LEUKODYSTROPHIES, LEUKOENCEPHALOPATHY)
MITOCHONDRIAL DNA DISORDERS-ALL (MTDNA)
PEDIATRIC NEUROTRANSMITTER DISEASE-ALL
SINGLE ENZYME DEFECTS-ALL (SINGLE-ENZYME)